FDA Approves Exondys51
September 19, 2016
19.09.2016-Sarepta Therapeutics Announces FDA Accelerated Approval of EXONDYS 51™ (eteplirsen) ...
Successfully accomplished/participated events (archive)
June 3, 2015
Visit the link to glance through a list of events organized/represented by Muscular Dystrophy Founda ...
Orphan Medicinal Product Designation for CAT - 1004
October 26, 2015
European Commission grants Orphan Medicinal Product designation for CAT-1004, Catabasis Pharmaceutic ...
Orphan Drug Designation for ARM210/S48168
December 9, 2015
ARMGO Pharma Receives FDA Orphan Drug Designation and Rare Pediatric Disease Designation for ARM210/ ...
Santhera Reports New Data for Raxone® (idebenone)
November 11, 2015
Santhera Reports New Data and Updates on Regulatory Filings for Raxone® (idebenone) in Duchenne ...
FDA Advisory Committee to Review Drisapersen
November 24, 2015
BioMarin Announces FDA Advisory Committee to Review Drisapersen for Treatment of Patients With Duche ...
Registration open for a residential program of rehabilitation & training
05/12/2015
Muscular Dystrophy Resource Center is currently admitting DMD children for a complete rehabilitation ...